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Orphan Drug
Orphan drug
Overview
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Orphan drugs
(56)
Ambrisentan
Eculizumab
Myozyme
Oncophage
Promacta
Promacta
Romiplostim
Sodium phenylbutyrate
Terguride
Vidaza
Xenazine
4-Aminopyridine
Acetohydroxamic acid
Anagrelide
Anti-CD22 immunotoxins
Bevacizumab
Bortezomib
Bosentan
Busulfan
Carboprost
Carglumic acid
Carmustine
Cilengitide
Cladribine
Clofazimine
Cysteamine
Dasatinib
Deferasirox
Eflornithine
Elesclomol
Fomivirsen
Gemtuzumab ozogamicin
Gusperimus
Icatibant
Idursulfase
Iloprost
Isofagomine tartrate
Mecasermin rinfabate
Miglustat
Mitotane
Nilotinib
Nitisinone
Paromomycin sulfate
Pazopanib
Pemtumomab
Plerixafor
Rifaximin
Rituximab
Sacrosidase
Sodium stibogluconate
Sorafenib
Stiripentol
Tiopronin
Tiratricol
Trabectedin
Vorinostat
Xyrem
more...
Drug discovery
Phase III clinical trials
Drug development
Pharmaceuticals policy
Prescription Drug User Fee Act
Food, Drug and Cosmetic Act
Antineoplastic drugs
Genasense
Dacogen
Glivec
Vidaza
Food and Drug Administration
(66)
Drug pipeline
Food and drug administration
Investigational new drug
New drug application
Abbreviated New Drug Application
Abbreviated New Drug Application
Bad Bug Book
Board of Tea Appeals
CSUCT
Center for Biologics Evaluation and Research
Center for Devices and Radiological Health
Center for Drug Evaluation and Research
Center for Food Safety and Applied Nutrition
Center for Veterinary Medicine
Class I recall
Commissioners of the Food and Drug Administration
Covered clinical study
Criticism of the Food and Drug Administration
Current Good Tissue Practices
Cytel
David Graham (epidemiologist)
Defense blood standard system
Design controls
Drug Coupon
Elixir sulfanilamide incident
Emergency Use Authorization
FDA Consumer
FDA Fast Track Development Program
FDA v. Brown & Williamson Tobacco Corp.
Food and Drug Administration Modernization Act of 1997
Food and Drug Administration images
Food code
Food, Drug and Cosmetic Act
Frances Oldham Kelsey
Hazard Analysis and Critical Control Points
JANUS clinical trial data repository
James Maryanski
John Nestor
Joshua Sharfstein
List of medicine contamination incidents
MSM blood donor controversy
MedWatch
Minor Use Animal Drug Program
National Center for Toxicological Research
National Drug Code
National Milk Laboratory Certification Program
Naval Ordnance Laboratory
Office of Criminal Investigations
Office of Regulatory Affairs
Orally disintegrating tablet
Personalized medicine
Pharma Fraud
Pharmaceutical drug
Phase III clinical trials
Premarket approval
Prescription Drug User Fee Act
Product licensing application
Pure Food and Drug Act
QSIT
Radura
SDTM
The Chemical Feast
The Food Defect Action Levels
Title 21 CFR Part 11
Unique Device Identification
United States v. Park
Vaccine Adverse Event Reporting System
more...
Pharmaceutical industry
(8)
New molecular entity
European Medicines Agency
Biopharmaceutical
Boxed warning
New drug application
New drug application
Phase III clinical trials
Lead compound
Drug development
more...
Chemotherapeutic agents
Tesetaxel
Bendamustine
Taxane
Biotechnology companies
Antigenics Inc.
BioMarin
Genzyme
Biogen Idec
Genmab
Celgene
Serono
Types of cancer
Cancer Drug
Renal cell carcinoma
Chronic lymphocytic leukemia
Acute promyelocytic leukemia
Gliomas
Pharmacology
(16)
Pharmaceuticals
Pralatrexate
Ptc124
Medicinal product
Cethromycin
Cethromycin
Biologics
Rufinamide
Genasense
Vidaza
New drug application
Dacogen
Phase III clinical trials
Lead compound
Terguride
Biopharmaceutical
Drug development
more...
Diseases and disorders
(13)
Rare diseases
Muckle wells syndrome
Pulmonary arterial hypertension
Myelodysplastic syndromes
Pompe disease
Pompe disease
Infantile spasms
Fabry disease
Fibrinogen deficiency
Choreia (disease)
Cancer Drug
Chronic lymphocytic leukemia
Acute promyelocytic leukemia
Gliomas
more...
See also
(20)
Orphan disease
ATryn
The Orphan
Antineoplaston
Cryopyrin
Cryopyrin
Professional certification
Rilonacept
Marshall Edwards
Nonsense mutations
European Organization for Rare Diseases
Supplementary protection certificate
Gamunex
Genta H. Holmes
FDA approval
National Organization for Rare Disorders
Epeius
Multiple myeloma patients
Acthar
Tegenero
Enzyme replacement therapy
more...
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